Elephant Man's Real Disease
In 1993 I was an honorary house officer at the National
Hospital for Neurological Disease and Stroke at Queen’s Square in
London. While I was there
I visited the Royal London Hospital where the skeletal remains of Mr.
Joseph Cary Merick have been kept.
Mr. Merick is a relatively famous Victorian who is probably
better known as the elephant man.
Sir Frederick Treves, a medical doctor, “discovered” Merick
in a carnival sideshow and he cared for him until his death in 1890.
The record of this doctor/patient relationship has provoked
some significant discussion about medical ethics, patients’ rights
and human dignity. For many years it was thought that Mr. Merick had suffered
from a severe form of neurofibromatosis (NF).
However, others theorized that he might have instead suffered
from a much rarer disorder called proteus syndrome. In 1986, Dr.
Michael Cohen at the University of Halifax in Nova Scotia, Canada
proposed that Mr. Merick had proteus syndrome. The radiologists at the
Royal London Hospital where Merick lived and his bones remain have now
substantiated this theory. By
taking plain film radiographs and CT scans of Merick’s skull they
were able to reveal characteristic findings of this non-inherited
disease caused by malfunctions in cell growth.
So, Mr. Merick did not, in fact, have neurofibromatosis.
Neurofibromatosis is a genetic disorder of the
nervous system that causes tumors to form on nerves anywhere in the
body. NF was first
referred to in the medical literature by Dr. Friedrich von
Recklinghausen and consequently has also come to be known as von
Recklinghausen’s disease. This
disorder may affect any ethnic group or race and it affects both sexes
equally. Even though this
is one of the most common genetic disorders in the United States, not
many people know of it.
NF is an autosomal dominant genetic condition meaning
that it is not contagious and only 50% of those affected with NF have
a prior family history. Also,
if a parent does not have NF he or she cannot pass it on to children.
NF is a nervous system disorder that can affect the body in
various ways, depending upon the type of NF.
There are two genetically distinct forms often referred to as
NF-1 and NF-2. NF-1
primarily affects the peripheral nervous system, which may result in a
multitude of small bumps or tumors in the small nerves within the
skin. NF-2 primarily
affects the central nervous system and may not have any outward
manifestations.
NF-2 is also sometimes know as bilateral acoustic NF
since it is associated with tumors of the acoustic nerves and this is
a much rarer condition occurring in only one out of 40 thousand
births. Patients with
this condition may have other tumors that involve cranial or spinal
nerves but tumors affecting the acoustic nerves are the hallmark for
this particular form of NF. People
with this condition may begin developing hearing loss beginning in
their teens or early twenties and this is often first noticed by
difficulty discriminating or understanding speech, especially when
talking on the telephone. Unfortunately,
these effects have some link to developmental problems, especially
learning disabilities, which are five times more common in patients
with NF than in the general population.
Since this is a genetic disorder, there are no cures
for this condition at this time.
Peripheral nerve tumors resulting from NF-1 are generally not
removed except in some unusual circumstances where they may cause some
functional impairment. Brain
and spinal tumors associated with NF-2 can often be removed
successfully and these are always easier to remove when discovered
early while the tumors are relatively smaller.
Since this is a genetic disorder, each child of a parent with
NF has a 50% chance of inheriting the gene and developing the
condition. There is also
a 50% chance that each child will not inherit the gene and will be
completely free of NF. The
type of NF that is inherited is always the same as that of the
affected parent although the severity and kind of manifestations
differ from person to person. NF can occur through a spontaneous gene mutation in
individuals who have no affected parents.
The National Neurofibromatosis Foundation was founded
fourteen years ago and has supported research that has discovered the
two genes responsible for NF. This
may hold some potential for some type of gene therapy to correct or
arrest this condition in the future.
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